Gene Therapy Cures Previously Incurable Genetic Disease in Clinical Trial

A groundbreaking gene therapy has successfully cured a previously incurable genetic disease in a clinical trial, representing a major advance in precision medicine. The treatment uses CRISPR gene editing to correct disease-causing mutations directly in patients' cells, eliminating the underlying cause of the condition rather than just managing symptoms. All 12 patients in the trial showed complete remission, with follow-up monitoring confirming the cure is permanent. The therapy works by extracting patients' cells, editing them to correct genetic defects, and reintroducing them into the body. This success opens the door for treating hundreds of other genetic diseases that were previously considered untreatable. The treatment received expedited regulatory approval, and similar therapies are now in development for other conditions. However, the high cost of personalized gene therapy raises questions about accessibility and healthcare equity.